genbehandling
Genbehandling, or gene therapy, is a medical approach that aims to treat or prevent disease by introducing, removing, or altering genetic material within a patient's cells. The goal can be to correct a faulty gene, compensate for a loss of function, or enhance cellular performance to combat disease. Gene therapy can involve altering DNA in living cells or modulating gene expression without changing the underlying DNA sequence.
Therapies are generally categorized as ex vivo and in vivo. In ex vivo approaches, cells are removed,
Delivery methods rely on vectors and editing tools. Viral vectors such as adeno-associated virus, lentivirus, and
Applications span inherited monogenic disorders, certain cancers through engineered immune cells, and other diseases where correcting