Geeniterapiassa

Geeniterapiassa is a concept related to gene therapy, a technique that uses genes to treat or prevent disease. This involves introducing genetic material into a person's cells to replace a missing or mutated gene, correct a faulty gene, or introduce a new gene that helps fight disease. Gene therapy is an experimental treatment and is still being developed for many conditions.

The goal of gene therapy is to treat diseases at their genetic root. This can be done in several ways. One approach is gene addition, where a functional copy of a gene is inserted into a cell to compensate for a gene that is not working correctly. Another method is gene correction, which aims to repair a mutated gene. Gene disruption is a third strategy, used to inactivate a gene that is functioning improperly.

Gene therapy can be applied ex vivo, meaning cells are removed from the body, genetically modified in a laboratory, and then returned to the patient. Alternatively, it can be performed in vivo, where therapeutic DNA is delivered directly into the patient's body. The delivery of genetic material typically relies on vectors, which are often modified viruses, to carry the therapeutic genes into target cells.

While promising, gene therapy faces challenges, including ensuring the safety and effectiveness of the treatments, as well as ethical considerations. Research is ongoing to overcome these hurdles and expand the potential applications of gene therapy for a range of genetic disorders, cancers, and infectious diseases.